A Rapamycin Pharmacogenomic Approach for the Childhood Dementia Niemann-Pick C
Journal
Journal of Inherited Metabolic Disease
ISSN
0141-8955
Date Issued
2026-06-18
Author(s)
Szenfeld, Benjamín
Las Heras, Macarena
Rubilar, Juan Carlos
Villarreal, Pablo
Olguín, Valeria
Cubillos, Francisco A.
Type
Article